Rare Disease Clinical Development & Access Summit

Rare Disease Clinical Development & Access Summit provides a unique opportunity for industry, researchers and patients to discuss common obstacles in clinical development, exchange best practices and case study learnings and explore opportunities to implement cost saving measures. Key topics addressed will include patient identification, recruitment and retention, novel study design and approaches, patient preference studies, preclinical collaborations and evolving technologies to enable adaptive trials. Patient-driven progress will also be highlighted through discussions of changes in the drug development paradigm.